Daphne H. Schoenmakers, Shanice Beerepoot, Laura A. Adang, Marije A. B. C. Asbreuk, Caroline G Bergner, Annette E. Bley, Jaap-Jan Boelens, Valeria Calbi, Alejandra Darling, Erik Eklund, Ángeles García Cazorla, Sabine W. Grønborg, Samuel Groeschel, Peter M. van Hasselt, Carla E. M. Hollak, Claire Horgan, Simon Jones, Tom de Koning, Lucia Laugwitz, Caroline Lindemans, Pascal Martin, Fanny Mochel, Andreas Øberg, Dipak Ram, Caroline Sevin, Ludger Schöls, Ayelet Zerem, Nicole I. Wolf, Francesca Fumagalli. Gene therapy in advanced metachromatic leukodystrophy: tempering expectations[J]. Protein&Cell, 2025, 16(1): 12-15. doi: 10.1093/procel/pwae065
Citation: Daphne H. Schoenmakers, Shanice Beerepoot, Laura A. Adang, Marije A. B. C. Asbreuk, Caroline G Bergner, Annette E. Bley, Jaap-Jan Boelens, Valeria Calbi, Alejandra Darling, Erik Eklund, Ángeles García Cazorla, Sabine W. Grønborg, Samuel Groeschel, Peter M. van Hasselt, Carla E. M. Hollak, Claire Horgan, Simon Jones, Tom de Koning, Lucia Laugwitz, Caroline Lindemans, Pascal Martin, Fanny Mochel, Andreas Øberg, Dipak Ram, Caroline Sevin, Ludger Schöls, Ayelet Zerem, Nicole I. Wolf, Francesca Fumagalli. Gene therapy in advanced metachromatic leukodystrophy: tempering expectations[J]. Protein&Cell, 2025, 16(1): 12-15. doi: 10.1093/procel/pwae065
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